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PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

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Page 1: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

PROCEDIMIENTO ESTUDIOS FASE IV

Unidad Cardiovascular

Novartis Argentina

Sergio Volman

Agosto 2008

ISPOR

Introduccioacuten

Enorme incremento de costo alocados en Investigacioacuten cliacutenica

Menor nuacutemero de drogas aprovadas

El costo de una nueva moleacutecula desde su descubrimiento hasta su comercializacioacuten es US$ 11 Tiempo 10-12 antildeos

No garantiza su eacutexito

Tiempo de patentes es menor dado que hay mayor desarrollo en investigacioacuten y menor en comercializacioacuten

Las empresas requieren altos MS en forma precoz

Autoridades Regulatorias

Exigen mayores evidencias acerca del perfil de seguridad de las drogas

Asegurar riesgo beneficio de la moleacutecula

Exigen la realizacioacuten de PMS Risk Management como soporte para su ingreso al mercado

4 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Sources of ldquoReal World Datardquo

EBM amp RCT placed at the top of the evidence hierarchy

bull Limited controlled experiment that not generalize to population settings or conditions not reflected in the trial

bull Impracticality of basing all of medicine on RCTs

bull Expensive

ISPOR ldquoReal Worldrdquo Task Force Report

bull Supplements to traditional registriation RCTs

bull Large simple trials (practical clinical trials)

bull Registries

bull Administrative data

bull Health surveys

bull Electronic records and medical chart reviews

bull httpwwwjusgovardatospersonales

bull httpwwwhc-virtualcom

5 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Ensayos Cliacutenicos Fase IV

1048698SujetosMaacutes de mil pacientes (Condiciones reales de uso)

1048698 ObjetivoSeguridad en condiciones reales de uso en poblaciones con

gran nuacutemero de sujetos

1048698 Informacioacuten que podemos obtenerOtros datos de eficacia

Datos de faacutermaco-economiacutea

Farmacovigilancia

Seguridad tras el empleo prolongado yo en grandes grupos

Deteccioacuten de efectos indeseables de baja yo muy baja frecuencia

6 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Poner de manifiesto sus efectos farmacodinaacutemicos recoger datos referentes a su absorcioacuten distribucioacuten metabolismo y excrecioacuten

Establecer su eficacia para una indicacioacuten terapeacuteutica profilaacutectica o diagnoacutestica

Conocer el perfil de sus reacciones adversas y establecer su seguridad

Reunir la suficiente informacioacuten documental que demuestre el adecuado balance beneficio-riesgo que la informacioacuten se ha obtenido de una forma eacutetica y metodoloacutegicamente adecuada y siguiendo la normativa vigente

Objetivo del Ensayo Cliacutenico

Definicioacuten PH IV study

ldquoSe define a los estudios de Fase IV como estudios cliacutenicos intervencionistas con un producto dentro de una indicacioacuten dosisesquema de dosificacioacuten aprobada para su publicacioacuten o bien para la exploracioacuten de nuevos usos siempre y cuando no haya intencioacuten de someter un nuevo registro

Clasificacioacuten de Estudios Cliacutenicos seguacuten su financiacioacuten

Tipo a Pagados por Casa Matriz a traveacutes de reembolsos Los pagos hechos para los estudios de este tipo no deben afectar los resultados internos

Tipo b Pagados de forma compartida por Casa Matriz y con recursos propios del paiacutes

Tipo c Todos los gastos generados por el estudio son pagados con recursos locales El Asesor Meacutedico en coordinacioacuten con Marketing elabora el presupuesto del estudio sobre la base de los gastos proyectados

Features Design Key Features

RCT (explanatiry)

Prospective Interventional

Gold Standard randomised blinded placebo-controlled to measure efficacy in highly selected patients with standardised and intense follow up

RCT (pragmaty)

Randomised open-label with a usual care control group to measure effectiveness in a broard patient population with follow up and less stringent inclusionexclusion criterion

Observational

Prospective observational

Non-randomised non interventional study that monitors a cohort(s) over time with possible inclusion of scheduled patient visit

Registry

Observational study of patients with a specific disease or receiving a specific treatment Described as peering over the shoulder of physicians and collecting data

Database analysis Chart review Model Retrospective

Captures patient data from an existing database

Captures patient data from patient records

Decisioacuten analytic framework that simulates the impact of intervention using multiple data sources

Phase IV Group

Important strategic questions to ask when selecting a post-

marketing study designbull What is the primary research question or primary endponit being evaluated pricing and reimbursement publication planning risk management pivotal data gap competitive positioning In other world who are the intended recipients of the study results Is the study focus registration or non-registration

bull Is the motivation for the study founded upon an important research question which may ultimately influence madical practice and benefit the patient

bull What studies have already been undertaken by competitors

bull What is the timeframe for relevance of the study results

bull What is the budget for the study

Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study

design Methodological Questionsbull Are comparative data required If yes

consider interventional

bull Do the study results need to have a high level of internal validity If yes consider interventional

bull Is there a need to measure a small difference in outcomes If yes consider interventional

bull Is there a need for longer term data If yes choose observational

bull Do the study results need to be generalisable If yes consider observational

bull Is there a need to estimates of drug utilisation and healthcare resources in real world practice If yes consider observational

bull At the outcome of interest rare events If yes consider observational

bull Are real worldnaturalistic effectiveness or safety results needed If yes consider observational

Practical questionsbull Do the outcomes of interest need to be

collected directly from the patients (for example patient reported outcome If yes consider either interventional or observational

bull Are the study results needed quickly If yes consider either interventional or retrospective

bull Is it a challenge to randomise patients to therapy or placebo due to ethical or recruitment issues If yes consider either interventional or retrospective

bull Are these sufficient historical data available in healthcare databases or in patient charts If yes consider retrospective

bull Is the budget limited os is it not feasible to conduct a resource-intensive study If yes consider either observational or retrospective

Ahora bien

bull Definimos disentildeo del estudio

bull Estrategia y metodologiacutea

bull Requerimientos regulatorios

bull Definir el nivel de intervencioacuten

Para estudios observacionalesEs una gran ambiguedad

ldquoLa gran ambiguumledadrdquo

bull La prescripcioacuten estaacute separada de la inclusioacuten en el estudio

bull Interrogatorios cuestionarios muestras de sangre Queacute son

bull Debe quedar en claro que es parte de la actividad diaria

bull Sin embargohelliphellip

Convencioacuten de Oviedo 2005

ldquocualquier intervencioacutenrdquo realizada durante un estudio cliacutenico que altere el bienestar humano que comprometa fisicamente o ponga en riesgo la salud psicoloacutegica de un paciente

15 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

16 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Create momentum

Create Noise

Build a community

Position your product or service

17 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Real worldUsage trends

Physicianrelationship

KOL relationship

Key physicianpresibers

Reimbursementsupport

Trade Publication

SymposiumPresentation

SalesRepresentatives

User meetingpresentation

Supplementssymposium

Peer review articules

New indication

Off Labelmonitoring

Support RMP

RegistriesPMSs PhIV Studies

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 2: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

Introduccioacuten

Enorme incremento de costo alocados en Investigacioacuten cliacutenica

Menor nuacutemero de drogas aprovadas

El costo de una nueva moleacutecula desde su descubrimiento hasta su comercializacioacuten es US$ 11 Tiempo 10-12 antildeos

No garantiza su eacutexito

Tiempo de patentes es menor dado que hay mayor desarrollo en investigacioacuten y menor en comercializacioacuten

Las empresas requieren altos MS en forma precoz

Autoridades Regulatorias

Exigen mayores evidencias acerca del perfil de seguridad de las drogas

Asegurar riesgo beneficio de la moleacutecula

Exigen la realizacioacuten de PMS Risk Management como soporte para su ingreso al mercado

4 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Sources of ldquoReal World Datardquo

EBM amp RCT placed at the top of the evidence hierarchy

bull Limited controlled experiment that not generalize to population settings or conditions not reflected in the trial

bull Impracticality of basing all of medicine on RCTs

bull Expensive

ISPOR ldquoReal Worldrdquo Task Force Report

bull Supplements to traditional registriation RCTs

bull Large simple trials (practical clinical trials)

bull Registries

bull Administrative data

bull Health surveys

bull Electronic records and medical chart reviews

bull httpwwwjusgovardatospersonales

bull httpwwwhc-virtualcom

5 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Ensayos Cliacutenicos Fase IV

1048698SujetosMaacutes de mil pacientes (Condiciones reales de uso)

1048698 ObjetivoSeguridad en condiciones reales de uso en poblaciones con

gran nuacutemero de sujetos

1048698 Informacioacuten que podemos obtenerOtros datos de eficacia

Datos de faacutermaco-economiacutea

Farmacovigilancia

Seguridad tras el empleo prolongado yo en grandes grupos

Deteccioacuten de efectos indeseables de baja yo muy baja frecuencia

6 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Poner de manifiesto sus efectos farmacodinaacutemicos recoger datos referentes a su absorcioacuten distribucioacuten metabolismo y excrecioacuten

Establecer su eficacia para una indicacioacuten terapeacuteutica profilaacutectica o diagnoacutestica

Conocer el perfil de sus reacciones adversas y establecer su seguridad

Reunir la suficiente informacioacuten documental que demuestre el adecuado balance beneficio-riesgo que la informacioacuten se ha obtenido de una forma eacutetica y metodoloacutegicamente adecuada y siguiendo la normativa vigente

Objetivo del Ensayo Cliacutenico

Definicioacuten PH IV study

ldquoSe define a los estudios de Fase IV como estudios cliacutenicos intervencionistas con un producto dentro de una indicacioacuten dosisesquema de dosificacioacuten aprobada para su publicacioacuten o bien para la exploracioacuten de nuevos usos siempre y cuando no haya intencioacuten de someter un nuevo registro

Clasificacioacuten de Estudios Cliacutenicos seguacuten su financiacioacuten

Tipo a Pagados por Casa Matriz a traveacutes de reembolsos Los pagos hechos para los estudios de este tipo no deben afectar los resultados internos

Tipo b Pagados de forma compartida por Casa Matriz y con recursos propios del paiacutes

Tipo c Todos los gastos generados por el estudio son pagados con recursos locales El Asesor Meacutedico en coordinacioacuten con Marketing elabora el presupuesto del estudio sobre la base de los gastos proyectados

Features Design Key Features

RCT (explanatiry)

Prospective Interventional

Gold Standard randomised blinded placebo-controlled to measure efficacy in highly selected patients with standardised and intense follow up

RCT (pragmaty)

Randomised open-label with a usual care control group to measure effectiveness in a broard patient population with follow up and less stringent inclusionexclusion criterion

Observational

Prospective observational

Non-randomised non interventional study that monitors a cohort(s) over time with possible inclusion of scheduled patient visit

Registry

Observational study of patients with a specific disease or receiving a specific treatment Described as peering over the shoulder of physicians and collecting data

Database analysis Chart review Model Retrospective

Captures patient data from an existing database

Captures patient data from patient records

Decisioacuten analytic framework that simulates the impact of intervention using multiple data sources

Phase IV Group

Important strategic questions to ask when selecting a post-

marketing study designbull What is the primary research question or primary endponit being evaluated pricing and reimbursement publication planning risk management pivotal data gap competitive positioning In other world who are the intended recipients of the study results Is the study focus registration or non-registration

bull Is the motivation for the study founded upon an important research question which may ultimately influence madical practice and benefit the patient

bull What studies have already been undertaken by competitors

bull What is the timeframe for relevance of the study results

bull What is the budget for the study

Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study

design Methodological Questionsbull Are comparative data required If yes

consider interventional

bull Do the study results need to have a high level of internal validity If yes consider interventional

bull Is there a need to measure a small difference in outcomes If yes consider interventional

bull Is there a need for longer term data If yes choose observational

bull Do the study results need to be generalisable If yes consider observational

bull Is there a need to estimates of drug utilisation and healthcare resources in real world practice If yes consider observational

bull At the outcome of interest rare events If yes consider observational

bull Are real worldnaturalistic effectiveness or safety results needed If yes consider observational

Practical questionsbull Do the outcomes of interest need to be

collected directly from the patients (for example patient reported outcome If yes consider either interventional or observational

bull Are the study results needed quickly If yes consider either interventional or retrospective

bull Is it a challenge to randomise patients to therapy or placebo due to ethical or recruitment issues If yes consider either interventional or retrospective

bull Are these sufficient historical data available in healthcare databases or in patient charts If yes consider retrospective

bull Is the budget limited os is it not feasible to conduct a resource-intensive study If yes consider either observational or retrospective

Ahora bien

bull Definimos disentildeo del estudio

bull Estrategia y metodologiacutea

bull Requerimientos regulatorios

bull Definir el nivel de intervencioacuten

Para estudios observacionalesEs una gran ambiguedad

ldquoLa gran ambiguumledadrdquo

bull La prescripcioacuten estaacute separada de la inclusioacuten en el estudio

bull Interrogatorios cuestionarios muestras de sangre Queacute son

bull Debe quedar en claro que es parte de la actividad diaria

bull Sin embargohelliphellip

Convencioacuten de Oviedo 2005

ldquocualquier intervencioacutenrdquo realizada durante un estudio cliacutenico que altere el bienestar humano que comprometa fisicamente o ponga en riesgo la salud psicoloacutegica de un paciente

15 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

16 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Create momentum

Create Noise

Build a community

Position your product or service

17 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Real worldUsage trends

Physicianrelationship

KOL relationship

Key physicianpresibers

Reimbursementsupport

Trade Publication

SymposiumPresentation

SalesRepresentatives

User meetingpresentation

Supplementssymposium

Peer review articules

New indication

Off Labelmonitoring

Support RMP

RegistriesPMSs PhIV Studies

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 3: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

Autoridades Regulatorias

Exigen mayores evidencias acerca del perfil de seguridad de las drogas

Asegurar riesgo beneficio de la moleacutecula

Exigen la realizacioacuten de PMS Risk Management como soporte para su ingreso al mercado

4 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Sources of ldquoReal World Datardquo

EBM amp RCT placed at the top of the evidence hierarchy

bull Limited controlled experiment that not generalize to population settings or conditions not reflected in the trial

bull Impracticality of basing all of medicine on RCTs

bull Expensive

ISPOR ldquoReal Worldrdquo Task Force Report

bull Supplements to traditional registriation RCTs

bull Large simple trials (practical clinical trials)

bull Registries

bull Administrative data

bull Health surveys

bull Electronic records and medical chart reviews

bull httpwwwjusgovardatospersonales

bull httpwwwhc-virtualcom

5 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Ensayos Cliacutenicos Fase IV

1048698SujetosMaacutes de mil pacientes (Condiciones reales de uso)

1048698 ObjetivoSeguridad en condiciones reales de uso en poblaciones con

gran nuacutemero de sujetos

1048698 Informacioacuten que podemos obtenerOtros datos de eficacia

Datos de faacutermaco-economiacutea

Farmacovigilancia

Seguridad tras el empleo prolongado yo en grandes grupos

Deteccioacuten de efectos indeseables de baja yo muy baja frecuencia

6 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Poner de manifiesto sus efectos farmacodinaacutemicos recoger datos referentes a su absorcioacuten distribucioacuten metabolismo y excrecioacuten

Establecer su eficacia para una indicacioacuten terapeacuteutica profilaacutectica o diagnoacutestica

Conocer el perfil de sus reacciones adversas y establecer su seguridad

Reunir la suficiente informacioacuten documental que demuestre el adecuado balance beneficio-riesgo que la informacioacuten se ha obtenido de una forma eacutetica y metodoloacutegicamente adecuada y siguiendo la normativa vigente

Objetivo del Ensayo Cliacutenico

Definicioacuten PH IV study

ldquoSe define a los estudios de Fase IV como estudios cliacutenicos intervencionistas con un producto dentro de una indicacioacuten dosisesquema de dosificacioacuten aprobada para su publicacioacuten o bien para la exploracioacuten de nuevos usos siempre y cuando no haya intencioacuten de someter un nuevo registro

Clasificacioacuten de Estudios Cliacutenicos seguacuten su financiacioacuten

Tipo a Pagados por Casa Matriz a traveacutes de reembolsos Los pagos hechos para los estudios de este tipo no deben afectar los resultados internos

Tipo b Pagados de forma compartida por Casa Matriz y con recursos propios del paiacutes

Tipo c Todos los gastos generados por el estudio son pagados con recursos locales El Asesor Meacutedico en coordinacioacuten con Marketing elabora el presupuesto del estudio sobre la base de los gastos proyectados

Features Design Key Features

RCT (explanatiry)

Prospective Interventional

Gold Standard randomised blinded placebo-controlled to measure efficacy in highly selected patients with standardised and intense follow up

RCT (pragmaty)

Randomised open-label with a usual care control group to measure effectiveness in a broard patient population with follow up and less stringent inclusionexclusion criterion

Observational

Prospective observational

Non-randomised non interventional study that monitors a cohort(s) over time with possible inclusion of scheduled patient visit

Registry

Observational study of patients with a specific disease or receiving a specific treatment Described as peering over the shoulder of physicians and collecting data

Database analysis Chart review Model Retrospective

Captures patient data from an existing database

Captures patient data from patient records

Decisioacuten analytic framework that simulates the impact of intervention using multiple data sources

Phase IV Group

Important strategic questions to ask when selecting a post-

marketing study designbull What is the primary research question or primary endponit being evaluated pricing and reimbursement publication planning risk management pivotal data gap competitive positioning In other world who are the intended recipients of the study results Is the study focus registration or non-registration

bull Is the motivation for the study founded upon an important research question which may ultimately influence madical practice and benefit the patient

bull What studies have already been undertaken by competitors

bull What is the timeframe for relevance of the study results

bull What is the budget for the study

Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study

design Methodological Questionsbull Are comparative data required If yes

consider interventional

bull Do the study results need to have a high level of internal validity If yes consider interventional

bull Is there a need to measure a small difference in outcomes If yes consider interventional

bull Is there a need for longer term data If yes choose observational

bull Do the study results need to be generalisable If yes consider observational

bull Is there a need to estimates of drug utilisation and healthcare resources in real world practice If yes consider observational

bull At the outcome of interest rare events If yes consider observational

bull Are real worldnaturalistic effectiveness or safety results needed If yes consider observational

Practical questionsbull Do the outcomes of interest need to be

collected directly from the patients (for example patient reported outcome If yes consider either interventional or observational

bull Are the study results needed quickly If yes consider either interventional or retrospective

bull Is it a challenge to randomise patients to therapy or placebo due to ethical or recruitment issues If yes consider either interventional or retrospective

bull Are these sufficient historical data available in healthcare databases or in patient charts If yes consider retrospective

bull Is the budget limited os is it not feasible to conduct a resource-intensive study If yes consider either observational or retrospective

Ahora bien

bull Definimos disentildeo del estudio

bull Estrategia y metodologiacutea

bull Requerimientos regulatorios

bull Definir el nivel de intervencioacuten

Para estudios observacionalesEs una gran ambiguedad

ldquoLa gran ambiguumledadrdquo

bull La prescripcioacuten estaacute separada de la inclusioacuten en el estudio

bull Interrogatorios cuestionarios muestras de sangre Queacute son

bull Debe quedar en claro que es parte de la actividad diaria

bull Sin embargohelliphellip

Convencioacuten de Oviedo 2005

ldquocualquier intervencioacutenrdquo realizada durante un estudio cliacutenico que altere el bienestar humano que comprometa fisicamente o ponga en riesgo la salud psicoloacutegica de un paciente

15 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

16 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Create momentum

Create Noise

Build a community

Position your product or service

17 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Real worldUsage trends

Physicianrelationship

KOL relationship

Key physicianpresibers

Reimbursementsupport

Trade Publication

SymposiumPresentation

SalesRepresentatives

User meetingpresentation

Supplementssymposium

Peer review articules

New indication

Off Labelmonitoring

Support RMP

RegistriesPMSs PhIV Studies

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 4: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

4 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Sources of ldquoReal World Datardquo

EBM amp RCT placed at the top of the evidence hierarchy

bull Limited controlled experiment that not generalize to population settings or conditions not reflected in the trial

bull Impracticality of basing all of medicine on RCTs

bull Expensive

ISPOR ldquoReal Worldrdquo Task Force Report

bull Supplements to traditional registriation RCTs

bull Large simple trials (practical clinical trials)

bull Registries

bull Administrative data

bull Health surveys

bull Electronic records and medical chart reviews

bull httpwwwjusgovardatospersonales

bull httpwwwhc-virtualcom

5 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Ensayos Cliacutenicos Fase IV

1048698SujetosMaacutes de mil pacientes (Condiciones reales de uso)

1048698 ObjetivoSeguridad en condiciones reales de uso en poblaciones con

gran nuacutemero de sujetos

1048698 Informacioacuten que podemos obtenerOtros datos de eficacia

Datos de faacutermaco-economiacutea

Farmacovigilancia

Seguridad tras el empleo prolongado yo en grandes grupos

Deteccioacuten de efectos indeseables de baja yo muy baja frecuencia

6 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Poner de manifiesto sus efectos farmacodinaacutemicos recoger datos referentes a su absorcioacuten distribucioacuten metabolismo y excrecioacuten

Establecer su eficacia para una indicacioacuten terapeacuteutica profilaacutectica o diagnoacutestica

Conocer el perfil de sus reacciones adversas y establecer su seguridad

Reunir la suficiente informacioacuten documental que demuestre el adecuado balance beneficio-riesgo que la informacioacuten se ha obtenido de una forma eacutetica y metodoloacutegicamente adecuada y siguiendo la normativa vigente

Objetivo del Ensayo Cliacutenico

Definicioacuten PH IV study

ldquoSe define a los estudios de Fase IV como estudios cliacutenicos intervencionistas con un producto dentro de una indicacioacuten dosisesquema de dosificacioacuten aprobada para su publicacioacuten o bien para la exploracioacuten de nuevos usos siempre y cuando no haya intencioacuten de someter un nuevo registro

Clasificacioacuten de Estudios Cliacutenicos seguacuten su financiacioacuten

Tipo a Pagados por Casa Matriz a traveacutes de reembolsos Los pagos hechos para los estudios de este tipo no deben afectar los resultados internos

Tipo b Pagados de forma compartida por Casa Matriz y con recursos propios del paiacutes

Tipo c Todos los gastos generados por el estudio son pagados con recursos locales El Asesor Meacutedico en coordinacioacuten con Marketing elabora el presupuesto del estudio sobre la base de los gastos proyectados

Features Design Key Features

RCT (explanatiry)

Prospective Interventional

Gold Standard randomised blinded placebo-controlled to measure efficacy in highly selected patients with standardised and intense follow up

RCT (pragmaty)

Randomised open-label with a usual care control group to measure effectiveness in a broard patient population with follow up and less stringent inclusionexclusion criterion

Observational

Prospective observational

Non-randomised non interventional study that monitors a cohort(s) over time with possible inclusion of scheduled patient visit

Registry

Observational study of patients with a specific disease or receiving a specific treatment Described as peering over the shoulder of physicians and collecting data

Database analysis Chart review Model Retrospective

Captures patient data from an existing database

Captures patient data from patient records

Decisioacuten analytic framework that simulates the impact of intervention using multiple data sources

Phase IV Group

Important strategic questions to ask when selecting a post-

marketing study designbull What is the primary research question or primary endponit being evaluated pricing and reimbursement publication planning risk management pivotal data gap competitive positioning In other world who are the intended recipients of the study results Is the study focus registration or non-registration

bull Is the motivation for the study founded upon an important research question which may ultimately influence madical practice and benefit the patient

bull What studies have already been undertaken by competitors

bull What is the timeframe for relevance of the study results

bull What is the budget for the study

Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study

design Methodological Questionsbull Are comparative data required If yes

consider interventional

bull Do the study results need to have a high level of internal validity If yes consider interventional

bull Is there a need to measure a small difference in outcomes If yes consider interventional

bull Is there a need for longer term data If yes choose observational

bull Do the study results need to be generalisable If yes consider observational

bull Is there a need to estimates of drug utilisation and healthcare resources in real world practice If yes consider observational

bull At the outcome of interest rare events If yes consider observational

bull Are real worldnaturalistic effectiveness or safety results needed If yes consider observational

Practical questionsbull Do the outcomes of interest need to be

collected directly from the patients (for example patient reported outcome If yes consider either interventional or observational

bull Are the study results needed quickly If yes consider either interventional or retrospective

bull Is it a challenge to randomise patients to therapy or placebo due to ethical or recruitment issues If yes consider either interventional or retrospective

bull Are these sufficient historical data available in healthcare databases or in patient charts If yes consider retrospective

bull Is the budget limited os is it not feasible to conduct a resource-intensive study If yes consider either observational or retrospective

Ahora bien

bull Definimos disentildeo del estudio

bull Estrategia y metodologiacutea

bull Requerimientos regulatorios

bull Definir el nivel de intervencioacuten

Para estudios observacionalesEs una gran ambiguedad

ldquoLa gran ambiguumledadrdquo

bull La prescripcioacuten estaacute separada de la inclusioacuten en el estudio

bull Interrogatorios cuestionarios muestras de sangre Queacute son

bull Debe quedar en claro que es parte de la actividad diaria

bull Sin embargohelliphellip

Convencioacuten de Oviedo 2005

ldquocualquier intervencioacutenrdquo realizada durante un estudio cliacutenico que altere el bienestar humano que comprometa fisicamente o ponga en riesgo la salud psicoloacutegica de un paciente

15 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

16 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Create momentum

Create Noise

Build a community

Position your product or service

17 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Real worldUsage trends

Physicianrelationship

KOL relationship

Key physicianpresibers

Reimbursementsupport

Trade Publication

SymposiumPresentation

SalesRepresentatives

User meetingpresentation

Supplementssymposium

Peer review articules

New indication

Off Labelmonitoring

Support RMP

RegistriesPMSs PhIV Studies

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 5: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

5 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Ensayos Cliacutenicos Fase IV

1048698SujetosMaacutes de mil pacientes (Condiciones reales de uso)

1048698 ObjetivoSeguridad en condiciones reales de uso en poblaciones con

gran nuacutemero de sujetos

1048698 Informacioacuten que podemos obtenerOtros datos de eficacia

Datos de faacutermaco-economiacutea

Farmacovigilancia

Seguridad tras el empleo prolongado yo en grandes grupos

Deteccioacuten de efectos indeseables de baja yo muy baja frecuencia

6 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Poner de manifiesto sus efectos farmacodinaacutemicos recoger datos referentes a su absorcioacuten distribucioacuten metabolismo y excrecioacuten

Establecer su eficacia para una indicacioacuten terapeacuteutica profilaacutectica o diagnoacutestica

Conocer el perfil de sus reacciones adversas y establecer su seguridad

Reunir la suficiente informacioacuten documental que demuestre el adecuado balance beneficio-riesgo que la informacioacuten se ha obtenido de una forma eacutetica y metodoloacutegicamente adecuada y siguiendo la normativa vigente

Objetivo del Ensayo Cliacutenico

Definicioacuten PH IV study

ldquoSe define a los estudios de Fase IV como estudios cliacutenicos intervencionistas con un producto dentro de una indicacioacuten dosisesquema de dosificacioacuten aprobada para su publicacioacuten o bien para la exploracioacuten de nuevos usos siempre y cuando no haya intencioacuten de someter un nuevo registro

Clasificacioacuten de Estudios Cliacutenicos seguacuten su financiacioacuten

Tipo a Pagados por Casa Matriz a traveacutes de reembolsos Los pagos hechos para los estudios de este tipo no deben afectar los resultados internos

Tipo b Pagados de forma compartida por Casa Matriz y con recursos propios del paiacutes

Tipo c Todos los gastos generados por el estudio son pagados con recursos locales El Asesor Meacutedico en coordinacioacuten con Marketing elabora el presupuesto del estudio sobre la base de los gastos proyectados

Features Design Key Features

RCT (explanatiry)

Prospective Interventional

Gold Standard randomised blinded placebo-controlled to measure efficacy in highly selected patients with standardised and intense follow up

RCT (pragmaty)

Randomised open-label with a usual care control group to measure effectiveness in a broard patient population with follow up and less stringent inclusionexclusion criterion

Observational

Prospective observational

Non-randomised non interventional study that monitors a cohort(s) over time with possible inclusion of scheduled patient visit

Registry

Observational study of patients with a specific disease or receiving a specific treatment Described as peering over the shoulder of physicians and collecting data

Database analysis Chart review Model Retrospective

Captures patient data from an existing database

Captures patient data from patient records

Decisioacuten analytic framework that simulates the impact of intervention using multiple data sources

Phase IV Group

Important strategic questions to ask when selecting a post-

marketing study designbull What is the primary research question or primary endponit being evaluated pricing and reimbursement publication planning risk management pivotal data gap competitive positioning In other world who are the intended recipients of the study results Is the study focus registration or non-registration

bull Is the motivation for the study founded upon an important research question which may ultimately influence madical practice and benefit the patient

bull What studies have already been undertaken by competitors

bull What is the timeframe for relevance of the study results

bull What is the budget for the study

Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study

design Methodological Questionsbull Are comparative data required If yes

consider interventional

bull Do the study results need to have a high level of internal validity If yes consider interventional

bull Is there a need to measure a small difference in outcomes If yes consider interventional

bull Is there a need for longer term data If yes choose observational

bull Do the study results need to be generalisable If yes consider observational

bull Is there a need to estimates of drug utilisation and healthcare resources in real world practice If yes consider observational

bull At the outcome of interest rare events If yes consider observational

bull Are real worldnaturalistic effectiveness or safety results needed If yes consider observational

Practical questionsbull Do the outcomes of interest need to be

collected directly from the patients (for example patient reported outcome If yes consider either interventional or observational

bull Are the study results needed quickly If yes consider either interventional or retrospective

bull Is it a challenge to randomise patients to therapy or placebo due to ethical or recruitment issues If yes consider either interventional or retrospective

bull Are these sufficient historical data available in healthcare databases or in patient charts If yes consider retrospective

bull Is the budget limited os is it not feasible to conduct a resource-intensive study If yes consider either observational or retrospective

Ahora bien

bull Definimos disentildeo del estudio

bull Estrategia y metodologiacutea

bull Requerimientos regulatorios

bull Definir el nivel de intervencioacuten

Para estudios observacionalesEs una gran ambiguedad

ldquoLa gran ambiguumledadrdquo

bull La prescripcioacuten estaacute separada de la inclusioacuten en el estudio

bull Interrogatorios cuestionarios muestras de sangre Queacute son

bull Debe quedar en claro que es parte de la actividad diaria

bull Sin embargohelliphellip

Convencioacuten de Oviedo 2005

ldquocualquier intervencioacutenrdquo realizada durante un estudio cliacutenico que altere el bienestar humano que comprometa fisicamente o ponga en riesgo la salud psicoloacutegica de un paciente

15 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

16 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Create momentum

Create Noise

Build a community

Position your product or service

17 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Real worldUsage trends

Physicianrelationship

KOL relationship

Key physicianpresibers

Reimbursementsupport

Trade Publication

SymposiumPresentation

SalesRepresentatives

User meetingpresentation

Supplementssymposium

Peer review articules

New indication

Off Labelmonitoring

Support RMP

RegistriesPMSs PhIV Studies

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 6: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

6 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Poner de manifiesto sus efectos farmacodinaacutemicos recoger datos referentes a su absorcioacuten distribucioacuten metabolismo y excrecioacuten

Establecer su eficacia para una indicacioacuten terapeacuteutica profilaacutectica o diagnoacutestica

Conocer el perfil de sus reacciones adversas y establecer su seguridad

Reunir la suficiente informacioacuten documental que demuestre el adecuado balance beneficio-riesgo que la informacioacuten se ha obtenido de una forma eacutetica y metodoloacutegicamente adecuada y siguiendo la normativa vigente

Objetivo del Ensayo Cliacutenico

Definicioacuten PH IV study

ldquoSe define a los estudios de Fase IV como estudios cliacutenicos intervencionistas con un producto dentro de una indicacioacuten dosisesquema de dosificacioacuten aprobada para su publicacioacuten o bien para la exploracioacuten de nuevos usos siempre y cuando no haya intencioacuten de someter un nuevo registro

Clasificacioacuten de Estudios Cliacutenicos seguacuten su financiacioacuten

Tipo a Pagados por Casa Matriz a traveacutes de reembolsos Los pagos hechos para los estudios de este tipo no deben afectar los resultados internos

Tipo b Pagados de forma compartida por Casa Matriz y con recursos propios del paiacutes

Tipo c Todos los gastos generados por el estudio son pagados con recursos locales El Asesor Meacutedico en coordinacioacuten con Marketing elabora el presupuesto del estudio sobre la base de los gastos proyectados

Features Design Key Features

RCT (explanatiry)

Prospective Interventional

Gold Standard randomised blinded placebo-controlled to measure efficacy in highly selected patients with standardised and intense follow up

RCT (pragmaty)

Randomised open-label with a usual care control group to measure effectiveness in a broard patient population with follow up and less stringent inclusionexclusion criterion

Observational

Prospective observational

Non-randomised non interventional study that monitors a cohort(s) over time with possible inclusion of scheduled patient visit

Registry

Observational study of patients with a specific disease or receiving a specific treatment Described as peering over the shoulder of physicians and collecting data

Database analysis Chart review Model Retrospective

Captures patient data from an existing database

Captures patient data from patient records

Decisioacuten analytic framework that simulates the impact of intervention using multiple data sources

Phase IV Group

Important strategic questions to ask when selecting a post-

marketing study designbull What is the primary research question or primary endponit being evaluated pricing and reimbursement publication planning risk management pivotal data gap competitive positioning In other world who are the intended recipients of the study results Is the study focus registration or non-registration

bull Is the motivation for the study founded upon an important research question which may ultimately influence madical practice and benefit the patient

bull What studies have already been undertaken by competitors

bull What is the timeframe for relevance of the study results

bull What is the budget for the study

Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study

design Methodological Questionsbull Are comparative data required If yes

consider interventional

bull Do the study results need to have a high level of internal validity If yes consider interventional

bull Is there a need to measure a small difference in outcomes If yes consider interventional

bull Is there a need for longer term data If yes choose observational

bull Do the study results need to be generalisable If yes consider observational

bull Is there a need to estimates of drug utilisation and healthcare resources in real world practice If yes consider observational

bull At the outcome of interest rare events If yes consider observational

bull Are real worldnaturalistic effectiveness or safety results needed If yes consider observational

Practical questionsbull Do the outcomes of interest need to be

collected directly from the patients (for example patient reported outcome If yes consider either interventional or observational

bull Are the study results needed quickly If yes consider either interventional or retrospective

bull Is it a challenge to randomise patients to therapy or placebo due to ethical or recruitment issues If yes consider either interventional or retrospective

bull Are these sufficient historical data available in healthcare databases or in patient charts If yes consider retrospective

bull Is the budget limited os is it not feasible to conduct a resource-intensive study If yes consider either observational or retrospective

Ahora bien

bull Definimos disentildeo del estudio

bull Estrategia y metodologiacutea

bull Requerimientos regulatorios

bull Definir el nivel de intervencioacuten

Para estudios observacionalesEs una gran ambiguedad

ldquoLa gran ambiguumledadrdquo

bull La prescripcioacuten estaacute separada de la inclusioacuten en el estudio

bull Interrogatorios cuestionarios muestras de sangre Queacute son

bull Debe quedar en claro que es parte de la actividad diaria

bull Sin embargohelliphellip

Convencioacuten de Oviedo 2005

ldquocualquier intervencioacutenrdquo realizada durante un estudio cliacutenico que altere el bienestar humano que comprometa fisicamente o ponga en riesgo la salud psicoloacutegica de un paciente

15 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

16 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Create momentum

Create Noise

Build a community

Position your product or service

17 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Real worldUsage trends

Physicianrelationship

KOL relationship

Key physicianpresibers

Reimbursementsupport

Trade Publication

SymposiumPresentation

SalesRepresentatives

User meetingpresentation

Supplementssymposium

Peer review articules

New indication

Off Labelmonitoring

Support RMP

RegistriesPMSs PhIV Studies

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 7: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

Definicioacuten PH IV study

ldquoSe define a los estudios de Fase IV como estudios cliacutenicos intervencionistas con un producto dentro de una indicacioacuten dosisesquema de dosificacioacuten aprobada para su publicacioacuten o bien para la exploracioacuten de nuevos usos siempre y cuando no haya intencioacuten de someter un nuevo registro

Clasificacioacuten de Estudios Cliacutenicos seguacuten su financiacioacuten

Tipo a Pagados por Casa Matriz a traveacutes de reembolsos Los pagos hechos para los estudios de este tipo no deben afectar los resultados internos

Tipo b Pagados de forma compartida por Casa Matriz y con recursos propios del paiacutes

Tipo c Todos los gastos generados por el estudio son pagados con recursos locales El Asesor Meacutedico en coordinacioacuten con Marketing elabora el presupuesto del estudio sobre la base de los gastos proyectados

Features Design Key Features

RCT (explanatiry)

Prospective Interventional

Gold Standard randomised blinded placebo-controlled to measure efficacy in highly selected patients with standardised and intense follow up

RCT (pragmaty)

Randomised open-label with a usual care control group to measure effectiveness in a broard patient population with follow up and less stringent inclusionexclusion criterion

Observational

Prospective observational

Non-randomised non interventional study that monitors a cohort(s) over time with possible inclusion of scheduled patient visit

Registry

Observational study of patients with a specific disease or receiving a specific treatment Described as peering over the shoulder of physicians and collecting data

Database analysis Chart review Model Retrospective

Captures patient data from an existing database

Captures patient data from patient records

Decisioacuten analytic framework that simulates the impact of intervention using multiple data sources

Phase IV Group

Important strategic questions to ask when selecting a post-

marketing study designbull What is the primary research question or primary endponit being evaluated pricing and reimbursement publication planning risk management pivotal data gap competitive positioning In other world who are the intended recipients of the study results Is the study focus registration or non-registration

bull Is the motivation for the study founded upon an important research question which may ultimately influence madical practice and benefit the patient

bull What studies have already been undertaken by competitors

bull What is the timeframe for relevance of the study results

bull What is the budget for the study

Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study

design Methodological Questionsbull Are comparative data required If yes

consider interventional

bull Do the study results need to have a high level of internal validity If yes consider interventional

bull Is there a need to measure a small difference in outcomes If yes consider interventional

bull Is there a need for longer term data If yes choose observational

bull Do the study results need to be generalisable If yes consider observational

bull Is there a need to estimates of drug utilisation and healthcare resources in real world practice If yes consider observational

bull At the outcome of interest rare events If yes consider observational

bull Are real worldnaturalistic effectiveness or safety results needed If yes consider observational

Practical questionsbull Do the outcomes of interest need to be

collected directly from the patients (for example patient reported outcome If yes consider either interventional or observational

bull Are the study results needed quickly If yes consider either interventional or retrospective

bull Is it a challenge to randomise patients to therapy or placebo due to ethical or recruitment issues If yes consider either interventional or retrospective

bull Are these sufficient historical data available in healthcare databases or in patient charts If yes consider retrospective

bull Is the budget limited os is it not feasible to conduct a resource-intensive study If yes consider either observational or retrospective

Ahora bien

bull Definimos disentildeo del estudio

bull Estrategia y metodologiacutea

bull Requerimientos regulatorios

bull Definir el nivel de intervencioacuten

Para estudios observacionalesEs una gran ambiguedad

ldquoLa gran ambiguumledadrdquo

bull La prescripcioacuten estaacute separada de la inclusioacuten en el estudio

bull Interrogatorios cuestionarios muestras de sangre Queacute son

bull Debe quedar en claro que es parte de la actividad diaria

bull Sin embargohelliphellip

Convencioacuten de Oviedo 2005

ldquocualquier intervencioacutenrdquo realizada durante un estudio cliacutenico que altere el bienestar humano que comprometa fisicamente o ponga en riesgo la salud psicoloacutegica de un paciente

15 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

16 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Create momentum

Create Noise

Build a community

Position your product or service

17 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Real worldUsage trends

Physicianrelationship

KOL relationship

Key physicianpresibers

Reimbursementsupport

Trade Publication

SymposiumPresentation

SalesRepresentatives

User meetingpresentation

Supplementssymposium

Peer review articules

New indication

Off Labelmonitoring

Support RMP

RegistriesPMSs PhIV Studies

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 8: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

Clasificacioacuten de Estudios Cliacutenicos seguacuten su financiacioacuten

Tipo a Pagados por Casa Matriz a traveacutes de reembolsos Los pagos hechos para los estudios de este tipo no deben afectar los resultados internos

Tipo b Pagados de forma compartida por Casa Matriz y con recursos propios del paiacutes

Tipo c Todos los gastos generados por el estudio son pagados con recursos locales El Asesor Meacutedico en coordinacioacuten con Marketing elabora el presupuesto del estudio sobre la base de los gastos proyectados

Features Design Key Features

RCT (explanatiry)

Prospective Interventional

Gold Standard randomised blinded placebo-controlled to measure efficacy in highly selected patients with standardised and intense follow up

RCT (pragmaty)

Randomised open-label with a usual care control group to measure effectiveness in a broard patient population with follow up and less stringent inclusionexclusion criterion

Observational

Prospective observational

Non-randomised non interventional study that monitors a cohort(s) over time with possible inclusion of scheduled patient visit

Registry

Observational study of patients with a specific disease or receiving a specific treatment Described as peering over the shoulder of physicians and collecting data

Database analysis Chart review Model Retrospective

Captures patient data from an existing database

Captures patient data from patient records

Decisioacuten analytic framework that simulates the impact of intervention using multiple data sources

Phase IV Group

Important strategic questions to ask when selecting a post-

marketing study designbull What is the primary research question or primary endponit being evaluated pricing and reimbursement publication planning risk management pivotal data gap competitive positioning In other world who are the intended recipients of the study results Is the study focus registration or non-registration

bull Is the motivation for the study founded upon an important research question which may ultimately influence madical practice and benefit the patient

bull What studies have already been undertaken by competitors

bull What is the timeframe for relevance of the study results

bull What is the budget for the study

Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study

design Methodological Questionsbull Are comparative data required If yes

consider interventional

bull Do the study results need to have a high level of internal validity If yes consider interventional

bull Is there a need to measure a small difference in outcomes If yes consider interventional

bull Is there a need for longer term data If yes choose observational

bull Do the study results need to be generalisable If yes consider observational

bull Is there a need to estimates of drug utilisation and healthcare resources in real world practice If yes consider observational

bull At the outcome of interest rare events If yes consider observational

bull Are real worldnaturalistic effectiveness or safety results needed If yes consider observational

Practical questionsbull Do the outcomes of interest need to be

collected directly from the patients (for example patient reported outcome If yes consider either interventional or observational

bull Are the study results needed quickly If yes consider either interventional or retrospective

bull Is it a challenge to randomise patients to therapy or placebo due to ethical or recruitment issues If yes consider either interventional or retrospective

bull Are these sufficient historical data available in healthcare databases or in patient charts If yes consider retrospective

bull Is the budget limited os is it not feasible to conduct a resource-intensive study If yes consider either observational or retrospective

Ahora bien

bull Definimos disentildeo del estudio

bull Estrategia y metodologiacutea

bull Requerimientos regulatorios

bull Definir el nivel de intervencioacuten

Para estudios observacionalesEs una gran ambiguedad

ldquoLa gran ambiguumledadrdquo

bull La prescripcioacuten estaacute separada de la inclusioacuten en el estudio

bull Interrogatorios cuestionarios muestras de sangre Queacute son

bull Debe quedar en claro que es parte de la actividad diaria

bull Sin embargohelliphellip

Convencioacuten de Oviedo 2005

ldquocualquier intervencioacutenrdquo realizada durante un estudio cliacutenico que altere el bienestar humano que comprometa fisicamente o ponga en riesgo la salud psicoloacutegica de un paciente

15 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

16 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Create momentum

Create Noise

Build a community

Position your product or service

17 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Real worldUsage trends

Physicianrelationship

KOL relationship

Key physicianpresibers

Reimbursementsupport

Trade Publication

SymposiumPresentation

SalesRepresentatives

User meetingpresentation

Supplementssymposium

Peer review articules

New indication

Off Labelmonitoring

Support RMP

RegistriesPMSs PhIV Studies

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 9: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

Features Design Key Features

RCT (explanatiry)

Prospective Interventional

Gold Standard randomised blinded placebo-controlled to measure efficacy in highly selected patients with standardised and intense follow up

RCT (pragmaty)

Randomised open-label with a usual care control group to measure effectiveness in a broard patient population with follow up and less stringent inclusionexclusion criterion

Observational

Prospective observational

Non-randomised non interventional study that monitors a cohort(s) over time with possible inclusion of scheduled patient visit

Registry

Observational study of patients with a specific disease or receiving a specific treatment Described as peering over the shoulder of physicians and collecting data

Database analysis Chart review Model Retrospective

Captures patient data from an existing database

Captures patient data from patient records

Decisioacuten analytic framework that simulates the impact of intervention using multiple data sources

Phase IV Group

Important strategic questions to ask when selecting a post-

marketing study designbull What is the primary research question or primary endponit being evaluated pricing and reimbursement publication planning risk management pivotal data gap competitive positioning In other world who are the intended recipients of the study results Is the study focus registration or non-registration

bull Is the motivation for the study founded upon an important research question which may ultimately influence madical practice and benefit the patient

bull What studies have already been undertaken by competitors

bull What is the timeframe for relevance of the study results

bull What is the budget for the study

Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study

design Methodological Questionsbull Are comparative data required If yes

consider interventional

bull Do the study results need to have a high level of internal validity If yes consider interventional

bull Is there a need to measure a small difference in outcomes If yes consider interventional

bull Is there a need for longer term data If yes choose observational

bull Do the study results need to be generalisable If yes consider observational

bull Is there a need to estimates of drug utilisation and healthcare resources in real world practice If yes consider observational

bull At the outcome of interest rare events If yes consider observational

bull Are real worldnaturalistic effectiveness or safety results needed If yes consider observational

Practical questionsbull Do the outcomes of interest need to be

collected directly from the patients (for example patient reported outcome If yes consider either interventional or observational

bull Are the study results needed quickly If yes consider either interventional or retrospective

bull Is it a challenge to randomise patients to therapy or placebo due to ethical or recruitment issues If yes consider either interventional or retrospective

bull Are these sufficient historical data available in healthcare databases or in patient charts If yes consider retrospective

bull Is the budget limited os is it not feasible to conduct a resource-intensive study If yes consider either observational or retrospective

Ahora bien

bull Definimos disentildeo del estudio

bull Estrategia y metodologiacutea

bull Requerimientos regulatorios

bull Definir el nivel de intervencioacuten

Para estudios observacionalesEs una gran ambiguedad

ldquoLa gran ambiguumledadrdquo

bull La prescripcioacuten estaacute separada de la inclusioacuten en el estudio

bull Interrogatorios cuestionarios muestras de sangre Queacute son

bull Debe quedar en claro que es parte de la actividad diaria

bull Sin embargohelliphellip

Convencioacuten de Oviedo 2005

ldquocualquier intervencioacutenrdquo realizada durante un estudio cliacutenico que altere el bienestar humano que comprometa fisicamente o ponga en riesgo la salud psicoloacutegica de un paciente

15 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

16 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Create momentum

Create Noise

Build a community

Position your product or service

17 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Real worldUsage trends

Physicianrelationship

KOL relationship

Key physicianpresibers

Reimbursementsupport

Trade Publication

SymposiumPresentation

SalesRepresentatives

User meetingpresentation

Supplementssymposium

Peer review articules

New indication

Off Labelmonitoring

Support RMP

RegistriesPMSs PhIV Studies

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 10: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

Important strategic questions to ask when selecting a post-

marketing study designbull What is the primary research question or primary endponit being evaluated pricing and reimbursement publication planning risk management pivotal data gap competitive positioning In other world who are the intended recipients of the study results Is the study focus registration or non-registration

bull Is the motivation for the study founded upon an important research question which may ultimately influence madical practice and benefit the patient

bull What studies have already been undertaken by competitors

bull What is the timeframe for relevance of the study results

bull What is the budget for the study

Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study

design Methodological Questionsbull Are comparative data required If yes

consider interventional

bull Do the study results need to have a high level of internal validity If yes consider interventional

bull Is there a need to measure a small difference in outcomes If yes consider interventional

bull Is there a need for longer term data If yes choose observational

bull Do the study results need to be generalisable If yes consider observational

bull Is there a need to estimates of drug utilisation and healthcare resources in real world practice If yes consider observational

bull At the outcome of interest rare events If yes consider observational

bull Are real worldnaturalistic effectiveness or safety results needed If yes consider observational

Practical questionsbull Do the outcomes of interest need to be

collected directly from the patients (for example patient reported outcome If yes consider either interventional or observational

bull Are the study results needed quickly If yes consider either interventional or retrospective

bull Is it a challenge to randomise patients to therapy or placebo due to ethical or recruitment issues If yes consider either interventional or retrospective

bull Are these sufficient historical data available in healthcare databases or in patient charts If yes consider retrospective

bull Is the budget limited os is it not feasible to conduct a resource-intensive study If yes consider either observational or retrospective

Ahora bien

bull Definimos disentildeo del estudio

bull Estrategia y metodologiacutea

bull Requerimientos regulatorios

bull Definir el nivel de intervencioacuten

Para estudios observacionalesEs una gran ambiguedad

ldquoLa gran ambiguumledadrdquo

bull La prescripcioacuten estaacute separada de la inclusioacuten en el estudio

bull Interrogatorios cuestionarios muestras de sangre Queacute son

bull Debe quedar en claro que es parte de la actividad diaria

bull Sin embargohelliphellip

Convencioacuten de Oviedo 2005

ldquocualquier intervencioacutenrdquo realizada durante un estudio cliacutenico que altere el bienestar humano que comprometa fisicamente o ponga en riesgo la salud psicoloacutegica de un paciente

15 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

16 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Create momentum

Create Noise

Build a community

Position your product or service

17 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Real worldUsage trends

Physicianrelationship

KOL relationship

Key physicianpresibers

Reimbursementsupport

Trade Publication

SymposiumPresentation

SalesRepresentatives

User meetingpresentation

Supplementssymposium

Peer review articules

New indication

Off Labelmonitoring

Support RMP

RegistriesPMSs PhIV Studies

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 11: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study

design Methodological Questionsbull Are comparative data required If yes

consider interventional

bull Do the study results need to have a high level of internal validity If yes consider interventional

bull Is there a need to measure a small difference in outcomes If yes consider interventional

bull Is there a need for longer term data If yes choose observational

bull Do the study results need to be generalisable If yes consider observational

bull Is there a need to estimates of drug utilisation and healthcare resources in real world practice If yes consider observational

bull At the outcome of interest rare events If yes consider observational

bull Are real worldnaturalistic effectiveness or safety results needed If yes consider observational

Practical questionsbull Do the outcomes of interest need to be

collected directly from the patients (for example patient reported outcome If yes consider either interventional or observational

bull Are the study results needed quickly If yes consider either interventional or retrospective

bull Is it a challenge to randomise patients to therapy or placebo due to ethical or recruitment issues If yes consider either interventional or retrospective

bull Are these sufficient historical data available in healthcare databases or in patient charts If yes consider retrospective

bull Is the budget limited os is it not feasible to conduct a resource-intensive study If yes consider either observational or retrospective

Ahora bien

bull Definimos disentildeo del estudio

bull Estrategia y metodologiacutea

bull Requerimientos regulatorios

bull Definir el nivel de intervencioacuten

Para estudios observacionalesEs una gran ambiguedad

ldquoLa gran ambiguumledadrdquo

bull La prescripcioacuten estaacute separada de la inclusioacuten en el estudio

bull Interrogatorios cuestionarios muestras de sangre Queacute son

bull Debe quedar en claro que es parte de la actividad diaria

bull Sin embargohelliphellip

Convencioacuten de Oviedo 2005

ldquocualquier intervencioacutenrdquo realizada durante un estudio cliacutenico que altere el bienestar humano que comprometa fisicamente o ponga en riesgo la salud psicoloacutegica de un paciente

15 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

16 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Create momentum

Create Noise

Build a community

Position your product or service

17 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Real worldUsage trends

Physicianrelationship

KOL relationship

Key physicianpresibers

Reimbursementsupport

Trade Publication

SymposiumPresentation

SalesRepresentatives

User meetingpresentation

Supplementssymposium

Peer review articules

New indication

Off Labelmonitoring

Support RMP

RegistriesPMSs PhIV Studies

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 12: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

Ahora bien

bull Definimos disentildeo del estudio

bull Estrategia y metodologiacutea

bull Requerimientos regulatorios

bull Definir el nivel de intervencioacuten

Para estudios observacionalesEs una gran ambiguedad

ldquoLa gran ambiguumledadrdquo

bull La prescripcioacuten estaacute separada de la inclusioacuten en el estudio

bull Interrogatorios cuestionarios muestras de sangre Queacute son

bull Debe quedar en claro que es parte de la actividad diaria

bull Sin embargohelliphellip

Convencioacuten de Oviedo 2005

ldquocualquier intervencioacutenrdquo realizada durante un estudio cliacutenico que altere el bienestar humano que comprometa fisicamente o ponga en riesgo la salud psicoloacutegica de un paciente

15 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

16 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Create momentum

Create Noise

Build a community

Position your product or service

17 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Real worldUsage trends

Physicianrelationship

KOL relationship

Key physicianpresibers

Reimbursementsupport

Trade Publication

SymposiumPresentation

SalesRepresentatives

User meetingpresentation

Supplementssymposium

Peer review articules

New indication

Off Labelmonitoring

Support RMP

RegistriesPMSs PhIV Studies

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 13: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

ldquoLa gran ambiguumledadrdquo

bull La prescripcioacuten estaacute separada de la inclusioacuten en el estudio

bull Interrogatorios cuestionarios muestras de sangre Queacute son

bull Debe quedar en claro que es parte de la actividad diaria

bull Sin embargohelliphellip

Convencioacuten de Oviedo 2005

ldquocualquier intervencioacutenrdquo realizada durante un estudio cliacutenico que altere el bienestar humano que comprometa fisicamente o ponga en riesgo la salud psicoloacutegica de un paciente

15 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

16 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Create momentum

Create Noise

Build a community

Position your product or service

17 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Real worldUsage trends

Physicianrelationship

KOL relationship

Key physicianpresibers

Reimbursementsupport

Trade Publication

SymposiumPresentation

SalesRepresentatives

User meetingpresentation

Supplementssymposium

Peer review articules

New indication

Off Labelmonitoring

Support RMP

RegistriesPMSs PhIV Studies

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 14: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

Convencioacuten de Oviedo 2005

ldquocualquier intervencioacutenrdquo realizada durante un estudio cliacutenico que altere el bienestar humano que comprometa fisicamente o ponga en riesgo la salud psicoloacutegica de un paciente

15 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

16 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Create momentum

Create Noise

Build a community

Position your product or service

17 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Real worldUsage trends

Physicianrelationship

KOL relationship

Key physicianpresibers

Reimbursementsupport

Trade Publication

SymposiumPresentation

SalesRepresentatives

User meetingpresentation

Supplementssymposium

Peer review articules

New indication

Off Labelmonitoring

Support RMP

RegistriesPMSs PhIV Studies

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 15: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

15 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

16 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Create momentum

Create Noise

Build a community

Position your product or service

17 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Real worldUsage trends

Physicianrelationship

KOL relationship

Key physicianpresibers

Reimbursementsupport

Trade Publication

SymposiumPresentation

SalesRepresentatives

User meetingpresentation

Supplementssymposium

Peer review articules

New indication

Off Labelmonitoring

Support RMP

RegistriesPMSs PhIV Studies

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 16: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

16 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Create momentum

Create Noise

Build a community

Position your product or service

17 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Real worldUsage trends

Physicianrelationship

KOL relationship

Key physicianpresibers

Reimbursementsupport

Trade Publication

SymposiumPresentation

SalesRepresentatives

User meetingpresentation

Supplementssymposium

Peer review articules

New indication

Off Labelmonitoring

Support RMP

RegistriesPMSs PhIV Studies

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 17: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

17 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Turning the marketing wheel

Real worldUsage trends

Physicianrelationship

KOL relationship

Key physicianpresibers

Reimbursementsupport

Trade Publication

SymposiumPresentation

SalesRepresentatives

User meetingpresentation

Supplementssymposium

Peer review articules

New indication

Off Labelmonitoring

Support RMP

RegistriesPMSs PhIV Studies

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 18: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

18 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Conclusion

The true challenge in strategically designing post-marketing research is to appropiately blend scientific objetives with commercial objetives while maintaining regulatory compliance Scientific and commercial objetives can co-exist in the same atudy if designed well

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 19: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

19 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Otros ISSUES a resolver

Costos del estudio

Analizar adecuadamente la validez interna y externa

Necesidad de monitoreo Gran impacto presupuestario

Falta de definicioacuten HA acerca de procedimientos a cumplir en estudios observacionales en fase IV

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 20: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

20 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Diapo de Articulo PDF

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 21: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

Alguna pregunta

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 22: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

COMITEacute DE ESTUDIOS CLINICOS

ASESOR MEDICO GERENTE DE PRODUCTOStudy Concept Sheet + Business Rationale + Trial Commitment Form

DIRECTOR MEDICO SUB REGIONAL REGIONALDIRECTOR DE MARKETING REGIONAL-Aprobacioacuten-Aprobacioacuten Condicional-Negacioacuten

ASESOR MEDICO Luego de la aprobacioacuten Regional sigue seguacuten Procedimientos globales y procedimientos locales descritos

-NIP MME02001 Local Phase IIIbIVc Trials

DIRECTOR MEDICOGERENTE DE MARKETING

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 23: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

AMCTL Seleccioacuten final de centros a traveacutes de un CEC

AMCROCRA

Visita de seleccioacuten de los centros

AMCTL Abre centro de costos-

Completa Form GSDC

DMAMCTL Se revisa el protocolo final protocol summary IC y CRF

DMICRO MngAM

Alocan presupuesto para recursos humanos

Coordinador de Fase IV (si necesario)

Training a todos los involucrados

AMCTLCRO

Prepara paquete regulatorio para centros y comunica a DRARegulatorioICRO

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 24: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

AMCRAIMS Reunioacuten de investigadores

AMCRA Enviacutea solicitud al TPA ingreso a base de registros puacuteblicos (SDCF)

Actualizacioacuten perioacutedica en IMPACT

CROCRAAM

Seguimiento y monitoreo del estudio de acuerdo a los procedimientos globales y locales aplicables

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005
Page 25: PROCEDIMIENTO ESTUDIOS FASE IV Unidad Cardiovascular Novartis Argentina Sergio Volman Agosto 2008 ISPOR

25 | Presentation Title | Presenter Name | Date | Subject | Business Use Only

Clarify some distinctions between registries andclinical trials

Clinical Trials Registries PMSs

An experimentObservational study

design it is a survey

Active intervemtiondoes not specify

treatments observational

Randomization Procedures Observe

Inclusion and exclusion criterias

few inclusion and exclusion criteria

few inclusion and exclusion criteria

Homogeneous group broad range of patientsbroad range of

patients

Adhere to a strict schedule of visits

Conduct protocol-specific tests and measurements

test and measurements a provider customarily uses Safety IMS

  • Slide 9
  • Important strategic questions to ask when selecting a post-marketing study design
  • Interventional observational or retrospective Methodological and practical questions to ask when selecting a post-marketing study design
  • Ahora bien
  • ldquoLa gran ambiguumledadrdquo
  • Convencioacuten de Oviedo 2005